Journal article Open Access

Lentiviral Hematopoietic Stem Cell Gene Therapy Benefits Metachromatic Leukodystrophy

Biffi, Alessandra; Montini, Eugenio; Lorioli, Laura; Cesani, Martina; Fumagalli, Francesca; Plati, Tiziana; Baldoli, Cristina; Martino, Sabata; Calabria, Andrea; Canale, Sabrina; Benedicenti, Fabrizio; Vallanti, Giuliana; Biasco, Luca; Leo, Simone; Kabbara, Nabil; Zanetti, Gianluigi; Rizzo, William B.; Mehta, Nalini A. L.; Cicalese, Maria Pia; Casiraghi, Miriam; Boelens, Jaap J.; Del Carro, Ubaldo; Dow, David J.; Schmidt, Manfred; Assanelli, Andrea; Neduva, Victor; Di Serio, Clelia; Stupka, Elia; Gardner, Jason; von Kalle, Christof; Bordignon, Claudio; Ciceri, Fabio; Rovelli, Attilio; Roncarolo, Maria Grazia; Aiuti, Alessandro; Sessa, Maria; Naldini, Luigi


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{
  "DOI": "10.1126/science.1233158", 
  "abstract": "<p>n/a</p>", 
  "author": [
    {
      "family": "Biffi, Alessandra"
    }, 
    {
      "family": "Montini, Eugenio"
    }, 
    {
      "family": "Lorioli, Laura"
    }, 
    {
      "family": "Cesani, Martina"
    }, 
    {
      "family": "Fumagalli, Francesca"
    }, 
    {
      "family": "Plati, Tiziana"
    }, 
    {
      "family": "Baldoli, Cristina"
    }, 
    {
      "family": "Martino, Sabata"
    }, 
    {
      "family": "Calabria, Andrea"
    }, 
    {
      "family": "Canale, Sabrina"
    }, 
    {
      "family": "Benedicenti, Fabrizio"
    }, 
    {
      "family": "Vallanti, Giuliana"
    }, 
    {
      "family": "Biasco, Luca"
    }, 
    {
      "family": "Leo, Simone"
    }, 
    {
      "family": "Kabbara, Nabil"
    }, 
    {
      "family": "Zanetti, Gianluigi"
    }, 
    {
      "family": "Rizzo, William B."
    }, 
    {
      "family": "Mehta, Nalini A. L."
    }, 
    {
      "family": "Cicalese, Maria Pia"
    }, 
    {
      "family": "Casiraghi, Miriam"
    }, 
    {
      "family": "Boelens, Jaap J."
    }, 
    {
      "family": "Del Carro, Ubaldo"
    }, 
    {
      "family": "Dow, David J."
    }, 
    {
      "family": "Schmidt, Manfred"
    }, 
    {
      "family": "Assanelli, Andrea"
    }, 
    {
      "family": "Neduva, Victor"
    }, 
    {
      "family": "Di Serio, Clelia"
    }, 
    {
      "family": "Stupka, Elia"
    }, 
    {
      "family": "Gardner, Jason"
    }, 
    {
      "family": "von Kalle, Christof"
    }, 
    {
      "family": "Bordignon, Claudio"
    }, 
    {
      "family": "Ciceri, Fabio"
    }, 
    {
      "family": "Rovelli, Attilio"
    }, 
    {
      "family": "Roncarolo, Maria Grazia"
    }, 
    {
      "family": "Aiuti, Alessandro"
    }, 
    {
      "family": "Sessa, Maria"
    }, 
    {
      "family": "Naldini, Luigi"
    }
  ], 
  "id": "23020", 
  "issued": {
    "date-parts": [
      [
        2013, 
        1, 
        1
      ]
    ]
  }, 
  "language": "eng", 
  "note": "Funded by the European Union. Part of the European Commission FP7 Open Access pilot.", 
  "title": "Lentiviral Hematopoietic Stem Cell Gene Therapy Benefits Metachromatic Leukodystrophy", 
  "type": "article-journal"
}
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