Journal article Open Access

Lentiviral Hematopoietic Stem Cell Gene Therapy Benefits Metachromatic Leukodystrophy

Biffi, Alessandra; Montini, Eugenio; Lorioli, Laura; Cesani, Martina; Fumagalli, Francesca; Plati, Tiziana; Baldoli, Cristina; Martino, Sabata; Calabria, Andrea; Canale, Sabrina; Benedicenti, Fabrizio; Vallanti, Giuliana; Biasco, Luca; Leo, Simone; Kabbara, Nabil; Zanetti, Gianluigi; Rizzo, William B.; Mehta, Nalini A. L.; Cicalese, Maria Pia; Casiraghi, Miriam; Boelens, Jaap J.; Del Carro, Ubaldo; Dow, David J.; Schmidt, Manfred; Assanelli, Andrea; Neduva, Victor; Di Serio, Clelia; Stupka, Elia; Gardner, Jason; von Kalle, Christof; Bordignon, Claudio; Ciceri, Fabio; Rovelli, Attilio; Roncarolo, Maria Grazia; Aiuti, Alessandro; Sessa, Maria; Naldini, Luigi


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@misc{biffi_alessandra_2013_23020,
  author       = {Biffi, Alessandra and
                  Montini, Eugenio and
                  Lorioli, Laura and
                  Cesani, Martina and
                  Fumagalli, Francesca and
                  Plati, Tiziana and
                  Baldoli, Cristina and
                  Martino, Sabata and
                  Calabria, Andrea and
                  Canale, Sabrina and
                  Benedicenti, Fabrizio and
                  Vallanti, Giuliana and
                  Biasco, Luca and
                  Leo, Simone and
                  Kabbara, Nabil and
                  Zanetti, Gianluigi and
                  Rizzo, William B. and
                  Mehta, Nalini A. L. and
                  Cicalese, Maria Pia and
                  Casiraghi, Miriam and
                  Boelens, Jaap J. and
                  Del Carro, Ubaldo and
                  Dow, David J. and
                  Schmidt, Manfred and
                  Assanelli, Andrea and
                  Neduva, Victor and
                  Di Serio, Clelia and
                  Stupka, Elia and
                  Gardner, Jason and
                  von Kalle, Christof and
                  Bordignon, Claudio and
                  Ciceri, Fabio and
                  Rovelli, Attilio and
                  Roncarolo, Maria Grazia and
                  Aiuti, Alessandro and
                  Sessa, Maria and
                  Naldini, Luigi},
  title        = {{Lentiviral Hematopoietic Stem Cell Gene Therapy 
                   Benefits Metachromatic Leukodystrophy}},
  month        = jan,
  year         = 2013,
  note         = {{Funded by the European Union. Part of the European 
                   Commission FP7 Open Access pilot.}},
  doi          = {10.1126/science.1233158},
  url          = {https://doi.org/10.1126/science.1233158}
}
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