Journal article Open Access
Biffi, Alessandra; Montini, Eugenio; Lorioli, Laura; Cesani, Martina; Fumagalli, Francesca; Plati, Tiziana; Baldoli, Cristina; Martino, Sabata; Calabria, Andrea; Canale, Sabrina; Benedicenti, Fabrizio; Vallanti, Giuliana; Biasco, Luca; Leo, Simone; Kabbara, Nabil; Zanetti, Gianluigi; Rizzo, William B.; Mehta, Nalini A. L.; Cicalese, Maria Pia; Casiraghi, Miriam; Boelens, Jaap J.; Del Carro, Ubaldo; Dow, David J.; Schmidt, Manfred; Assanelli, Andrea; Neduva, Victor; Di Serio, Clelia; Stupka, Elia; Gardner, Jason; von Kalle, Christof; Bordignon, Claudio; Ciceri, Fabio; Rovelli, Attilio; Roncarolo, Maria Grazia; Aiuti, Alessandro; Sessa, Maria; Naldini, Luigi
@misc{biffi_alessandra_2013_23020, author = {Biffi, Alessandra and Montini, Eugenio and Lorioli, Laura and Cesani, Martina and Fumagalli, Francesca and Plati, Tiziana and Baldoli, Cristina and Martino, Sabata and Calabria, Andrea and Canale, Sabrina and Benedicenti, Fabrizio and Vallanti, Giuliana and Biasco, Luca and Leo, Simone and Kabbara, Nabil and Zanetti, Gianluigi and Rizzo, William B. and Mehta, Nalini A. L. and Cicalese, Maria Pia and Casiraghi, Miriam and Boelens, Jaap J. and Del Carro, Ubaldo and Dow, David J. and Schmidt, Manfred and Assanelli, Andrea and Neduva, Victor and Di Serio, Clelia and Stupka, Elia and Gardner, Jason and von Kalle, Christof and Bordignon, Claudio and Ciceri, Fabio and Rovelli, Attilio and Roncarolo, Maria Grazia and Aiuti, Alessandro and Sessa, Maria and Naldini, Luigi}, title = {{Lentiviral Hematopoietic Stem Cell Gene Therapy Benefits Metachromatic Leukodystrophy}}, month = jan, year = 2013, note = {{Funded by the European Union. Part of the European Commission FP7 Open Access pilot.}}, doi = {10.1126/science.1233158}, url = {https://doi.org/10.1126/science.1233158} }
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