Journal article Open Access

Lentiviral Hematopoietic Stem Cell Gene Therapy Benefits Metachromatic Leukodystrophy

Biffi, Alessandra; Montini, Eugenio; Lorioli, Laura; Cesani, Martina; Fumagalli, Francesca; Plati, Tiziana; Baldoli, Cristina; Martino, Sabata; Calabria, Andrea; Canale, Sabrina; Benedicenti, Fabrizio; Vallanti, Giuliana; Biasco, Luca; Leo, Simone; Kabbara, Nabil; Zanetti, Gianluigi; Rizzo, William B.; Mehta, Nalini A. L.; Cicalese, Maria Pia; Casiraghi, Miriam; Boelens, Jaap J.; Del Carro, Ubaldo; Dow, David J.; Schmidt, Manfred; Assanelli, Andrea; Neduva, Victor; Di Serio, Clelia; Stupka, Elia; Gardner, Jason; von Kalle, Christof; Bordignon, Claudio; Ciceri, Fabio; Rovelli, Attilio; Roncarolo, Maria Grazia; Aiuti, Alessandro; Sessa, Maria; Naldini, Luigi


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    <title>Lentiviral Hematopoietic Stem Cell Gene Therapy Benefits Metachromatic Leukodystrophy</title>
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  <publisher>INFN Open Access Repository</publisher>
  <publicationYear>2013</publicationYear>
  <subjects>
    <subject>FP7</subject>
    <subject>European Commission</subject>
    <subject>EC</subject>
    <subject>Health</subject>
    <subject>SP2-Ideas</subject>
    <subject>ERC</subject>
    <subject>SP1-Cooperation</subject>
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  <dates>
    <date dateType="Issued">2013-01-01</date>
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  <language>en</language>
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    <description descriptionType="Other">Funded by the European Union. Part of the European Commission FP7 Open Access pilot.</description>
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