Journal article Open Access

Lentiviral Hematopoietic Stem Cell Gene Therapy Benefits Metachromatic Leukodystrophy

Biffi, Alessandra; Montini, Eugenio; Lorioli, Laura; Cesani, Martina; Fumagalli, Francesca; Plati, Tiziana; Baldoli, Cristina; Martino, Sabata; Calabria, Andrea; Canale, Sabrina; Benedicenti, Fabrizio; Vallanti, Giuliana; Biasco, Luca; Leo, Simone; Kabbara, Nabil; Zanetti, Gianluigi; Rizzo, William B.; Mehta, Nalini A. L.; Cicalese, Maria Pia; Casiraghi, Miriam; Boelens, Jaap J.; Del Carro, Ubaldo; Dow, David J.; Schmidt, Manfred; Assanelli, Andrea; Neduva, Victor; Di Serio, Clelia; Stupka, Elia; Gardner, Jason; von Kalle, Christof; Bordignon, Claudio; Ciceri, Fabio; Rovelli, Attilio; Roncarolo, Maria Grazia; Aiuti, Alessandro; Sessa, Maria; Naldini, Luigi


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  <dc:creator>Biffi, Alessandra</dc:creator>
  <dc:creator>Montini, Eugenio</dc:creator>
  <dc:creator>Lorioli, Laura</dc:creator>
  <dc:creator>Cesani, Martina</dc:creator>
  <dc:creator>Fumagalli, Francesca</dc:creator>
  <dc:creator>Plati, Tiziana</dc:creator>
  <dc:creator>Baldoli, Cristina</dc:creator>
  <dc:creator>Martino, Sabata</dc:creator>
  <dc:creator>Calabria, Andrea</dc:creator>
  <dc:creator>Canale, Sabrina</dc:creator>
  <dc:creator>Benedicenti, Fabrizio</dc:creator>
  <dc:creator>Vallanti, Giuliana</dc:creator>
  <dc:creator>Biasco, Luca</dc:creator>
  <dc:creator>Leo, Simone</dc:creator>
  <dc:creator>Kabbara, Nabil</dc:creator>
  <dc:creator>Zanetti, Gianluigi</dc:creator>
  <dc:creator>Rizzo, William B.</dc:creator>
  <dc:creator>Mehta, Nalini A. L.</dc:creator>
  <dc:creator>Cicalese, Maria Pia</dc:creator>
  <dc:creator>Casiraghi, Miriam</dc:creator>
  <dc:creator>Boelens, Jaap J.</dc:creator>
  <dc:creator>Del Carro, Ubaldo</dc:creator>
  <dc:creator>Dow, David J.</dc:creator>
  <dc:creator>Schmidt, Manfred</dc:creator>
  <dc:creator>Assanelli, Andrea</dc:creator>
  <dc:creator>Neduva, Victor</dc:creator>
  <dc:creator>Di Serio, Clelia</dc:creator>
  <dc:creator>Stupka, Elia</dc:creator>
  <dc:creator>Gardner, Jason</dc:creator>
  <dc:creator>von Kalle, Christof</dc:creator>
  <dc:creator>Bordignon, Claudio</dc:creator>
  <dc:creator>Ciceri, Fabio</dc:creator>
  <dc:creator>Rovelli, Attilio</dc:creator>
  <dc:creator>Roncarolo, Maria Grazia</dc:creator>
  <dc:creator>Aiuti, Alessandro</dc:creator>
  <dc:creator>Sessa, Maria</dc:creator>
  <dc:creator>Naldini, Luigi</dc:creator>
  <dc:date>2013-01-01</dc:date>
  <dc:description>n/a</dc:description>
  <dc:identifier>https://www.openaccessrepository.it/record/23020</dc:identifier>
  <dc:identifier>10.1126/science.1233158</dc:identifier>
  <dc:language>eng</dc:language>
  <dc:relation>url:https://www.openaccessrepository.it/communities/itmirror</dc:relation>
  <dc:rights>info:eu-repo/semantics/openAccess</dc:rights>
  <dc:subject>FP7</dc:subject>
  <dc:subject>European Commission</dc:subject>
  <dc:subject>EC</dc:subject>
  <dc:subject>Health</dc:subject>
  <dc:subject>SP2-Ideas</dc:subject>
  <dc:subject>ERC</dc:subject>
  <dc:subject>SP1-Cooperation</dc:subject>
  <dc:title>Lentiviral Hematopoietic Stem Cell Gene Therapy Benefits Metachromatic Leukodystrophy</dc:title>
  <dc:type>info:eu-repo/semantics/article</dc:type>
  <dc:type>publication-article</dc:type>
</oai_dc:dc>
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